AAV9-mediated MYBPC3 gene therapy with optimized expression cassette enhances cardiac function and survival in MYBPC3 cardiomyopathy models
2025
·
Amara Greer-Short, Anna Greenwood, Elena Leon, Tawny Qureshi, Konor von Kraut, Justin Wong, Jonathan Tsui, Christopher Reid, Ze Cheng, Emilee Easter, Jin Yang, Jaclyn Ho, Stephanie Steltzer, Ana Budan, Marie Cho, Rishikesan Chandrakumar, Olga Cisne-Thompson, Charles Feathers, Tae Chung, Neshel Rodriguez, Samantha Jones, Chris Alleyne-Levy, Jun Liu, Frank Jing, William Prince, JianMin Lin, Kathryn Ivey, Whittemore Tingley, Timothy Hoey, Laura Lombardi
·
Nature Communications
Publication Details
- Journal
- Nature Communications
- Volume
- 16
- Issue
- 1
- Publisher
- Springer Science and Business Media LLC
- ISSN
- 2041-1723